Gene Therapy Program | Conditions We Treat

Open and enrolling gene therapy clinical trials

Currently, we have 7 open and enrolling clinical trials. In addition, we are a certified treatment center for providing the FDA-approved CAR T-cell therapy called KYMRIAH™ for relapsed B-cell acute lymphoblastic leukemia (ALL) and for the gene replacement therapy called for Zolgensma® for spinal muscular atrophy (SMA).