Research at Boston Children's Hospital
The research enterprise at Boston Children’s Hospital, comprising more than 3,000 researchers, is the world’s largest at a pediatric center. Our work is fueled by a deep understanding of disease biology coupled with world-class discovery platforms, including genetics and genomics, gene editing, bioinformatics, proteomics, bioengineering, image analysis, biobanks, disease-specific stem cell lines, and a range of animal models. We have special expertise in rare disease discovery, a robust Translational Research Program and large, diverse patient populations for clinical research and trials.
Featured news and research
Mending injured hearts: Lessons from newborns?
We can’t regenerate our heart tissue, but newborns can do so in mouse models. The lab of Miao Cui, PhD, seeks to capture those regeneration-friendly factors and harness them therapeutically.
The journey to a treatment for hereditary spastic paraplegia
A parent and the lab of Darius Ebrahimi-Fakhari, MD, PhD, team up and discover a small-molecule drug that could treat several forms of hereditary spastic paraplegia.
Robert Langer, ScD receives Kavli Award in Nanoscience
Robert Langer, ScD, chairs the Research Committee on our Board of Trustees. A longtime MIT faculty member, he also made contributions to angiogenesis in the lab of the late Judah Folkman, MD.
Rising stars in research
Meet some of our scientists and the projects they hope to advance.